Tag Archives: Non-Viral Gene Delivery

Engineered extracellular vesicles delivered full-length DMD mRNA to skeletal muscle, restoring dystrophin expression and improving muscle function in preclinical Duchenne muscular dystrophy models...

Spot Biosystems announced its launch from stealth with $40 million in venture financing, along with preclinical research published in Nature Biomedical Engineering and an ongoing first-in-human clinical trial for Duchenne muscular dystrophy. The company is developing a non-viral extracellular vesicle ...